ACR Meeting Abstracts

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Abstracts tagged "Outcome measures"

  • Abstract Number: 030 • 2023 Pediatric Rheumatology Symposium

    International Validation of the Total Morbidity Score for Juvenile Localized Scleroderma: 2023 Update

    Christina ZIgler1, Debra Henke2, Clare Pain3, Hanna Lythgoe3, Kaveh Ardalan2, Kathryn Torok4 and Suzanne Li5, 1Duke, Durham, NC, 2Duke University School of Medicine, Durham, NC, 3Alder Hey Children's NHS Foundation Trust, Liverpool, United Kingdom, 4University of Pittsburgh, Pittsburgh, PA, 5Hackensack Meridian School of Medicine, Joseph M. Sanzari Children's Hospital, Hackensack, NJ

    Background/Purpose: Juvenile localized scleroderma (jLS) is a rare condition causing inflammation and fibrosis that may impair health-related quality of life (HRQoL). Recent studies demonstrate extracutaneous…
  • Abstract Number: 039 • 2023 Pediatric Rheumatology Symposium

    Towards the Definition of Cutoff Values for Disease Activity States in Systemic JIA Using the Systemic Juvenile Arthritis Disease Activity Score

    Ana Isabel Rebollo-Giménez1, Yulia Vyzhga2, Luca Carlini3, Silvia Rosina4, Elisa Patrone1, Maria Katsikas5, Claudia Magalhaes6, Dalia El-Ghoneimy7, Yasser El Miedany8, Raju Khubchandani9, Priyankar Pal10, Gabriele Simonini11, Giovanni Filocamo12, Maurizio Gattinara13, Fabrizio De Benedetti14, Davide Montin15, Adele Civino16, Muatasem Alsuweiti17, Valda Stanevicha18, Vyacheslav Chasnyk19, Ekaterina Alexeeva20, Sulaiman M Al-Mayouf21, Soamarat Vilaiyuk22 and Angelo Ravelli23, 1IRCCS Istituto Giannina Gaslini, UOC Reumatologia e Malattie Infiammatorie, Genova, Italy, 2IRCCS Istituto Giannina Gaslini, UOC Reumatologia e Malattia Infiammatorie, Genova, Italy, 3IRCCS Istituto Giannina Gaslini, UOC Reumatologia e Malattie Autoinfiammatorie, Genova, Italy, 4IRCCS Istituto Giannina Gaslini, Genova, Italy, 5Hospital de Pediatria Juan P. Garrahan, Department of Immunology/Rheumatology, Buenos Aires, Argentina, 6São Paulo State University, Pediatric Rheumatology Division, Botucatu, Brazil, 7Children's Hospital, Ain Shams University, Pediatric Allergy, Immunology and Rheumatology Unit, Cairo, Egypt, 8Ain Shams University, Department of Rheumatology and Rehabilitation, Cairo, Egypt, 9Jaslok Hospital and Research Centre, Department of Paediatrics, Mumbai, India, 10Institute of Child Health, Pediatric medicine, Kolkata, India, Kolkata, India, 11IRCCS Meyer Children’s Hospital, Rheumatology Unit, Florence, Italy, 12Fondazione IRCCS Ca' Granda-Ospedale Maggiore Policlinico, Pediatric Rheumatology, Milano, Italy, 13Istituto Gaetano Pini, Rheumatology Unit, Milano, Italy,, Genova, 14Division of Rheumatology, IRCCS Ospedale Pediatrico Bambino Gesù, Roma, Italy, 15Regina Margherita Children Hospital, Immunology and Rheumatology Unit, Turin, Italy, 16Ospedale Vito Fazzi, Paediatric Immunology/Rheumatology Service, Lecce, Italy, 17King Hussein Medical Center, Department of Pediatrics - Pediatric Allergy, Immunology & Rheumatology Clinic, Amman, Jordan, 18University Children Hospital, Department of Pediatrics, Riga, Latvia, 19Saint-Petersburg State Pediatric Medical University, Department of Hospital Pediatrics, St. Petersburg, Russia, 20Federal State Autonomous Institution “National Medical Research Center of Children's Health”, Ministry of Health of the Russian Federation, Moscow, Russia, 21King Faisal Specialist Hospital & Research Center, Alfaisal University, Department of Pediatric Rheumatology, Riyadh, Saudi Arabia, 22Mahidol University Faculty of Medicine, Ramathibodi Hospital Department of Pediatrics, Bangkok, Thailand, 23IRRCS Istituto Giannina Gaslini and Università degli Studi di Genova, Genova, Italy

    Background/Purpose: Systemic juvenile idiopathic arthritis (sJIA) accounts up to 15% of all patients with JIA and is distinctfrom the other disease categories due to the…
  • Abstract Number: 064 • 2023 Pediatric Rheumatology Symposium

    Towards the Development of Composite Parent-Centered Disease Activity Scores for Juvenile Dermatomyositis

    Silvia Rosina1, Ana Isabel Rebollo-Giménez2, Letizia Tarantola3, Roberta Naddei4, Alessandro Consolaro2, Angela Pistorio5 and Angelo Ravelli6, 1IRCCS Istituto Giannina Gaslini, Genova, Italy, 2IRCCS Istituto Giannina Gaslini, UOC Reumatologia e Malattie Infiammatorie, Genova, Italy, 3Università degli Studi di Genova, Dipartimento di Neuroscienze, Riabilitazione, Oftalmologia, Genetica e Scienze Materno-Infantili (DiNOGMI), Genova, Italy, 4Università degli Studi di Napoli Federico II, Dipartimento di Scienze Mediche Traslazionali, Napoli, Italy, 5IRCCS Istituto Giannina Gaslini, Direzione Scientifica, Genova, Italy, 6IRRCS Istituto Giannina Gaslini and Università degli Studi di Genova, Genova, Italy

    Background/Purpose: Increasing attention has been recently paid to the development of parent- and child-centered composite DAS for the assessment of health status of children with…
  • Abstract Number: 091 • 2023 Pediatric Rheumatology Symposium

    Achieving Remission in Childhood-onset Systemic Lupus Erythematosus: Rapid Implementation of an EMR-integrated Dashboard to Measure Disease Activity and Remission Rates

    Kaleo Ede1, Nikita Goswami2, Elisa Wershba2, Michael Shishov2, Samantha Casselman2, Pierina Ortiz2 and Vinay Vaidya2, 1Phoenix Children's Hosptial; University of Arizona College of Medicine- Phoenix, Phoenix, AZ, 2Phoenix Children's Hospital, Phoenix, AZ

    Background/Purpose: Children with childhood-onset systemic lupus erythematosus (cSLE) experience more severe disease than their adult counterparts, in addition to high rates of clinical depressive symptoms…
  • Abstract Number: 093 • 2023 Pediatric Rheumatology Symposium

    Comparison Between Induction with Rituximab and Cyclophosphamide in Treatment of Childhood-Onset ANCA-Associated Vasculitis

    Samuel Gagne1, Kimberly Morishita2, Else Bosman3, Vidya Sivaraman4, David Cabral5, For the PedVas Investigators6 and Brett Klamer7, 1Nationwide Children's Hospital, Columbus, OH, 2University of British Columbia, Vancouver, BC, Canada, 3UBC, Vancouver, BC, Canada, 4Nationwide Children's Hospital/ The Ohio State University, Columbus, OH, 5BC Children's Hospital and University of British Columbia, Vancouver, BC, Canada, 6PedVas, 7Biostatistics Resource at Nationwide Children’s Hospital (BRANCH), Nationwide Children’s Hospital, Columbus, OH

    Background/Purpose: Granulomatosis with polyangiitis (GPA) and microscopic polyangiitis (MPA) are a group vasculitides with significant morbidity and mortality requiring toxic therapy. Clinical trials in adults…
  • Abstract Number: 120 • 2023 Pediatric Rheumatology Symposium

    The Brazilian Registry of Juvenile Dermatomyositis (JDM): I- Onset Clinical Features and Disease Activity Scores by DAS-20 over 2-Years-Follow Up

    Beatriz Carneiro1, Adriana Elias1, Teresa Robazzi2, Ana Julia Moraes3, Sheila Oliveira4, Flavio Sztajnbok5, Luciana Carvalho6, Luciana Marques7, Silvana Sacchetti8, Maria Teresa Terreri9, Simone Appenzelle10, Roberto Marini11, Andre Cavalcante12, Marcia Bandeira13, Cristina Magalhaes14, Melissa Fraga15, Iloite Scheibel16, Isabela Daud1, Darcisio Antonio17, Claudio Len18, Clovis Silva19, Taciana Fernandes17 and Claudia Magalhaes20, 1Instituto da Criança - Universidade de São Paulo (USP), São Paulo, Brazil, 2Universidade Federal da Bahia, Brazil, 3Universidade Federal do Para, Brazil, 4Universidade Federal do Rio de janeiro, Rio de Janeiro, 5Universidade Estadual do Rio de Janeiro, Rio de Janeiro, Brazil, 6Universidade de Sao Paulo- Ribeirao Preto, São Paulo, Brazil, 7Hospital Albert Sabin, Brazil, 8Santa Casa de Sao Paulo, Brazil, 9UNIFESP, São Paulo, Brazil, 10University of Campinas, Campinas, Sao Paulo, Brazil, 11UNICAMP, São Paulo, Brazil, 12Hospital Materno-Infantil de Goiania, Brazil, 13Hospital Pequeno Principe- Curitiba, Brazil, 14Hospital Jose de Alencar - Brasilia, Brazil, 15Hospital Darcy Vargas, Brazil, 16Hospital Conceição de Porto Alegre, Brazil, 17Universidade Estadual Paulista (UNESP) Botucatu, Brazil, 18Universidade Federal de São Paulo - Unifesp, São Paulo, Brazil, 19Universidade de São Paulo, São Paulo, Brazil, 20São Paulo State University, Pediatric Rheumatology Division, Botucatu, Brazil

    Background/Purpose: A national registry was set up, enrolling new onset JDM cases in 18 hospitals, during 3-years (2015-2018) with 2-years follow up, in a low…
  • Abstract Number: 005 • 2023 Pediatric Rheumatology Symposium

    Real-World Application of the Pediatric Glucocorticoid Toxicity Index in Children with Lupus Nephritis: A Feasibility and Initial Validation Study

    Emily Zhang1, Gabrielle Alonzi1, Madeline Hlobik1, Esra Meidan1, Mindy Lo1, Olha Halyabar2, Melissa Hazen1, Ezra Cohen3, Lauren Henderson1, Siobhan Case4, Margaret Chang1, Camille Frank1, Ankana Daga1, Jonathan Hausmann5, Ahmad Bakhsh1, Liyoung Kim1, Daniel Ibanez1, Holly Wobma1, Mia Chandler6, Fatma Dedeoglu1, Robert Sundel1, Peter Nigrovic1, Karen Costenbader7, Mary Beth Son1 and Joyce Chang1, 1Boston Children's Hospital, Boston, MA, 2Children's Hospital/Boston Medical Center, Boston, MA, 3Boston Medical Center, Boston, MA, 4Brigham and Women's Hospital, Boston Children's Hospital, Boston, MA, 5Boston Children's Hospital / Massachusetts General Hospital, Boston, MA, 6Boston Children's Hospital; Brigham and Women's Hospital, Boston, MA, 7Brigham and Women's Hospital/ Harvard Medical School, Boston, MA

    Background/Purpose: The morbidity of chronic glucocorticoid (GC) use is rarely captured as a standardized clinical outcome in pediatric rheumatic conditions. The newly developed pediatric glucocorticoid…
  • Abstract Number: 028 • 2023 Pediatric Rheumatology Symposium

    Achieving Medication-Free Remission in Juvenile Dermatomyositis

    Harneet Ghumman1, Ilaria Maccora2, Hermine Brunner1, Amy Cassedy3, Mekibib Altaye2, Asra Firdous1, Alexei Grom1, Daniel Lovell1, Angela Merritt1, Megan Quinlan-Waters1 and Sheila Angeles-Han2, 1Cincinnati Children's Hospital Medical Center, Cincinnati, OH, 2Cincinnati Children's Hospital, Cincinnati, OH, 3Cincinnati Children's Hospital Medical Center, Cincinnati, OH

    Background/Purpose: Juvenile dermatomyositis (JDM) is characterized by symmetric proximal muscle weakness, distinct rash, and a risk for calcinosis. Systemic immunosuppression is needed. Evidence is limited…
  • Abstract Number: 0077 • ACR Convergence 2022

    Rheumatoid Arthritis – Are We Getting to Target?

    myint Thway1, Gurjit S. Kaeley2, Karishma Ramsubeik3, Laurie Ramrattan1, Lilian Otalora Rojas4 and Sukhraj Singh1, 1University of Florida-Jacksonville, Jacksonville, FL, 2UF COM-J, Ponte Vedra Beach, FL, 3University of Florida, Jacksonville, FL, 4University of Florida, Ponte Vedra Beach, FL

    Background/Purpose: Low disease activity (LDA) is a key goal in treating Rheumatoid arthritis, but implementing the treat to target approach in clinical practice has been…
  • Abstract Number: 0285 • ACR Convergence 2022

    Characteristics and Outcomes of Patients with Rheumatoid Arthritis Treated with Upadacitinib in a Global Real-World Setting

    Roberto Felice Caporali1, Jayeshkumar Patel2, Oliver Howell3, sander strengholt4, Hannah Jones3 and Peter Taylor5, 1University of Milan, Milano, Italy, 2AbbVie, Inc., North Chicago, IL, 3Adelphi Real World, Bollington, United Kingdom, 4AbbVie, Inc., Abcoude, Netherlands, 5University of Oxford, Oxford, United Kingdom

    Background/Purpose: Upadacitinib (UPA), a Janus kinase inhibitor, is a newly approved advanced therapy for patients (pts) with rheumatoid arthritis (RA), thus real-world evidence is lacking.…
  • Abstract Number: 0722 • ACR Convergence 2022

    Cardiovascular and Oncologic Outocomes of Anti-TNF Alfa and JAK Inhibitors in Patients with Rheumatoid and Psoriatic Arthritis. Real World Data and Insights of BIOBADASAR 3.0 Registry

    Alejandro Brigante1, Rosana Quintana2, Carolina Isnardi3, Karen Roberts4, Gimena Gomez5, Maria Haye Salinas6, Enrique Soriano7, Guillermo Pons-Estel8, Maria De la Vega8, Osvaldo kerzberg7, Julieta Gamba7, Anastasia Secco9, Gustavo Citera10, Cesar Graf7, Veronica Savio11, Maria de los Angeles Gallardo7, Nora Aste7, Mercedes A Garcia12, Gustavo Casado7, Carla Gobbi7, Graciela Gomez7, Joan Manuel Dapeña13, Guillermo Berbotto7, Malena Viola7, Jonathan Rebak7, Diana Dubinsky7, Veronica Saurit14, Ingrid Petkovic7, Ana Bertoli7, Erika Catay7, C Leoni7, Ida Elena Exeni7, Bernardo Pons-Estel15, Sergio Paira7, GH Bovea Castelblanco7, Mercedes De la Sota7, Dora Pereira7, Gustavo Medina7, Amelia Granel7, Maria s Larroude7, Analia Patricia Alvarez7, Santiago Agüero16, Cecilia Pisoni17, Monica Sacnun7 and Edson Velozo18, 1UNISAR, Lobos, Argentina, 2Centro Regional de Enfermedades Autoinmunes y Reumáticas. Grupo Oroño (GO CREAR) and Research Unit Argentine Society of Rheumatology, Buenos Aires, Argentina, 3SAR-COVID Coordinator, Research Unit Argentine Society of Rheumatology, Buenos Aires, Argentina, 4UNISAR, Rosario, Argentina, 5Sanatorio Guemes, Buenos Aires, Argentina, 6UNLAR, La Rioja, Argentina, 7On behalf of the BIOBADASAR 3.0 registry, Buenos Aires, Argentina, 8Argentine Society of Rheumatology, Buenos Aires, Argentina, 9Rivadavia Hospital, Buenos Aires, Argentina, 10Instituto de Rehabilitación Psicofísica (IREP), Buenos Aires, Argentina, 11Hospital Córdoba; Consultora Integral de Salud CMP, Cordoba, Argentina, 12HIGA San Martin, La Plata, Argentina, 13Hospital General de Agudos Dr. Enrique Tornu, Buenos Aires, Argentina, 14Hospital Privado Universitario, Cordoba, Argentina, 15Grupo Oroño - Centro Regional de Enfermedades Autoinmunes y Reumáticas (GO-CREAR), Rosario, Argentina, 16Centro de Rehabilitación Dr Mauricio Figueroa, Catamarca, Argentina, 17CEMIC- Centro de Educación Médica e Investigaciones Clínicas, Buenos Aires, Argentina, 18SAR COVID Investigator, Caba

    Background/Purpose: Major adverse cardiovascular events (MACE) and neoplasms are a concern in autoimmune diseases. RA and PsA are diseases where inflammation plays a key role…
  • Abstract Number: 1084 • ACR Convergence 2022

    Rituximab versus Cyclophosphamide for Induction Therapy in Granulomatosis with Polyangiitis: A Target Trial Emulation Study

    Xavier Puéchal1, Michele Iudici2, Elodie Perrodeau3, bernard bonnotte4, Francois Lifermann5, Thomas Le Gallou6, Alexandre Karras7, Claire Blanchard-Delaunay8, Thomas Quéméneur9, Achille Aouba10, Olivier Aumaître11, Vincent Cottin12, Mohamed Hamidou13, Marc Ruivard11, Pascal Cohen1, Luc Mouthon1, Loïc Guillevin1, Philippe Ravaud3, Raphaël Porcher3 and Benjamin Terrier1, 1National Referral Center for Rare Systemic Autoimmune Diseases, Cochin Hospital, Paris, France, 2Division of Rheumatology, Geneva University Hospitals, Geneva, Switzerland, 3Université Paris Cité, Hôtel-Dieu, Paris, France, 4Centre Hospitalo-Universitaire de Dijon, Dijon, France, 5Dax Hospital, Dax, France, 6Rennes Sud University Hospital, Rennes, France, 7HEGP, Paris, France, 8Niort Hospital, Niort, France, 9Valenciennes Hospital, Valenciennes, France, 10Department of Internal Medicine, UR4650 PSIR, Normandie Univ, UNICAEN, CHU de Caen Normandie, Caen, France, 11Clermont Ferrand University Hospital, Clermont-Ferrand, France, 12Coordinating Reference Center for Rare Pulmonary Diseases, Louis Pradel Hospital, University of Lyon, INRAE, Lyon, France, 13Nantes University Hospital, Nantes, France

    Background/Purpose: Randomized controlled trials showed rituximab (RTX)'s non-inferiority to cyclophosphamide (CYC) for induction therapy of ANCA-associated vasculitis and neither treatment was favoured in granulomatosis with…
  • Abstract Number: 1388 • ACR Convergence 2022

    Updating and Validating the Rheumatic Disease Comorbidity Index to Incorporate ICD-10 Diagnostic Codes

    Anthony Dolomisiewicz1, Hanifah Ali2, Punyasha Roul3, Yangyuna Yang1, Grant Cannon4, Joshua Baker5, Ted Mikuls6, Kaleb Michaud1 and Bryant England1, 1University of Nebraska Medical Center, Omaha, NE, 2UNMC, Omaha, 3UNMC, Omaha, NE, 4Salt Lake City VA, Salt Lake city, 5University of Pennsylvania and Corporal Michael J. Crescenz VA Medical Center, Philadelphia, 6Division of Rheumatology, University of Nebraska Medical Center, Omaha, NE

    Background/Purpose: The Rheumatic Disease Comorbidity Index (RDCI) was designed to quantify comorbidity burden for risk stratification of health outcomes in patients with rheumatic disease. Developed…
  • Abstract Number: 1847 • ACR Convergence 2022

    Differences in Key Patient-reported Outcome Domains Identified by the Patient Acceptable Symptom State in the Adult SAPHO and Chronic Nonbacterial Osteomyelitis Observational Study (The SAPHO-CNO Study)

    Aleksander Lenert1, Robyn Domsic2, Karmela Kim Chan3, Melissa Oliver4, Jisna Paul5, Courtney Kremer6, Emma Leisinger1, Svjetlana Dolovcak7, Sandy D. Hong8, Aruni Jayatilleke9, Petar Lenert7, T. Shawn Sato1, Samir Shah10, Shima Yasin11, Yongdong (Dan) Zhao12, Daniel Solomon13, Jonathan Templin1 and Polly Ferguson11, 1University of Iowa, Iowa City, IA, 2University of Pittsburgh, Pittsburgh, PA, 3Hospital for Special Surgery, New York, NY, 4Indiana University School of Medicine, Indianapolis, IN, 5Ohio State University Hospital, Dublin, OH, 6University of Iowa Stead Family Children's Hospital, Solna, IA, 7University of Iowa Hospitals and Clinics, Iowa City, IA, 8University of Iowa Stead Family Children's Hospital, Iowa City, IA, 9Temple University, PHILADELPHIA, PA, 10Tufts Medical Center, Boston, MA, 11University of Iowa Carver College of Medicine, Iowa City, IA, 12University of Washington, Redmond, WA, 13Brigham and Women's Hospital, Boston, MA

    Background/Purpose: Incorporating patient perspectives of their disease state is needed for disease activity assessment in adults with SAPHO syndrome and chronic nonbacterial osteomyelitis (CNO). The…
  • Abstract Number: 2105 • ACR Convergence 2022

    Comparison of the Systemic Lupus International Collaborating Clinics Frailty Index (SLICC-FI) and the FRAIL Scale for Identifying Frailty Among Individuals with Systemic Lupus Erythematosus

    Alexandra Legge1, Sarah Lieber2 and John Hanly3, 1Arthritis Research Canada, Dalhousie University, Halifax, NS, Canada, 2Hospital for Special Surgery, New York, NY, 3Division of Rheumatology, Queen Elizabeth II Health Sciences Center (Nova Scotia Rehabilitation Site) and Dalhousie University, Halifax, NS, Canada

    Background/Purpose: Frailty is associated with increased risk of adverse health outcomes in SLE. Multiple definitions for frailty exist, and how best to measure frailty in…
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